Sarepta Therapeutics’ long-awaited confirmatory study of two of its ‘exon-skipping’ therapies for forms of Duchenne muscular dystrophy failed to meet its primary endpoint, the company announced Monday.
But despite that, the company plans to ask …
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The ESSENCE trial of Sarepta’s Vyondys 53 and Amondys 45 failed to hit its objective, placing their FDA accelerated approvals at risk.
Figuring out how to transport genetic medicines to the right parts of the body remains one of the great technical challenges constraining CRISPR’s potential. Now,
CDMO executives say they are unfazed about the wave of pharma companies boosting their internal manufacturing capacity as they onshore to the US, noting this
CDR-Life has inked a second licensing pact with Boehringer Ingelheim, as the Zurich-based startup will work with the German drug company in a ripe area
															Sarepta Therapeutics’ long-awaited confirmatory study of two of its ‘exon-skipping’ therapies for forms of Duchenne muscular dystrophy failed to meet its primary endpoint, the company announced Monday.
But despite that, the company plans to ask …