The FDA on Tuesday approved a gene therapy for a rare immune disease called Wiskott-Aldrich syndrome, for which patients have little options besides a bone marrow transplant.
The gene therapy will be marketed as Waskyra …
Flow Neuroscience has secured FDA approval for FL-100, the first at-home brain stimulation device for major depressive disorder.
Agreement has been reached on the reform of EU pharma legislation, but industry thinks it does not go far enough to restore the bloc’s global
Umoja Biopharma, one of the most well-capitalized developers of in vivo CAR-T therapy, is delaying its first clinical readout from its China-based first trial. The
Share price falls of 90% are mercifully rare in biopharma — but as Rezolute discovered Thursday, not entirely unknown. The wholesale failure of the Phase
Rhythm Pharmaceuticals unveiled initial data from a mid-stage study of its MC4R agonist in patients with a rare disease that causes excessive hunger. The biotech’s
The FDA on Tuesday approved a gene therapy for a rare immune disease called Wiskott-Aldrich syndrome, for which patients have little options besides a bone marrow transplant.
The gene therapy will be marketed as Waskyra …